An informal place to help support people afflicted with FMD. Sunday, October 8, 2017. Dr W Park, Chief of Vascular Surgery at Cleveland Clinic Abu Dhabi.

2nd IRDiRC Conference - Shenzhen. 7 9 November, 2014. Futian Sheraton Hotel, Shenzhen, China. The educational track on 7-8 November. A training course on genetics on 9 November. A matchmaking workshop to facilitate collaboration between clinicians and scientists. Key Features of the Conference. Access to big data and samples platforms, current discoveries, and advanced technologies.

WE ARE STAYING IN AMSTERDAM! The Orphan Drugs Summit, will be back for the 7th edition, again in Amsterdam. After five successful years in Copenhagen, we moved to Amsterdam last year, And we are happy to announce that we are staying in Holland, by popular demand! With a more than ten per cent compound annual growth rate, the prescription sales in the orphan sector is growing at twice the rate of the overall prescription market. Fast changing national and regional regulations.

Their behaviors, motivations, and unmet needs. Siren Interactive Infographic Highlights Role of Rare Disease in Precision Medicine. Read our on-going series on Diagnosis. Connect with us on Facebook. Learn about the Siren culture. Catch up on rare disease news.

A blog about Cystic Fibrosis and Kalydeco. Info for CFs on Kalydeco. 5 years of Kalydeco! February 17, 2015. I am having another procedure for my obstructed blood vessel tomorrow, but thought I would write about how everything is going with kalydeco in the meantime.

A Blog by Mohamed Fathi SAFFAR Pharm. D;Docteur es-sciences Pharmaceutiques;GMP-Inspector; Director at NATIONAL LABORATORY FOR DRUG CONTROL. Originally posted on New Drug Approvals.

Previously, infusions were biweekly. It still wipes me out when I get home. Another New Drug; More Guinea Pigging for Me.

This is just part one of the steps to giving factor. Walter has severe hemophilia A and continues to do things like this.